The Billings Livestock Commission hosted the sixth annual Calves to Cure to help raise money and awareness for Duchenne ...
The U.S. Food and Drug Administration has approved Zevra Therapeutics' drug for a rare and fatal genetic disorder, making it ...
The Los Angeles County Department of Public Health is looking into two human cases of a rare parasitic infection that comes ...
Despite being a flight away, Colleen's quick return home was met with relief as Dr. Alp Sener, Division Head of Urology at ...
For example, this one vet chose to care for this pitbull puppy despite the fact that she had a rare and very serious disease ...
Multiple system atrophy, or MSA, is a rare neurodegenerative disorder with symptoms akin to ALS or Parkinson’s disease in the ...
A House committee on Wednesday passed a bill to renew a program aimed at aiding development of drugs for rare diseases in ...
An Oscar-nominated actor recently spoke exclusively to PEOPLE about his adult son with a rare disease. It inspired a Rocky ...
Parents pushed for years for treatments for the neuron disease Niemann-Pick type C. After setbacks, one drug now has FDA ...
After pushing back the decision date for Applied Therapeutics’ metabolic disorder drug govorestat, the FDA has now decided ...
A 23-year-old Florida woman has been temporarily blinded and bruised after allegedly being required to receive multiple ...
Ongoing research is exploring new molecular targets and targeted therapies for this challenging disease.